
Andreas Heuer
Research team manager

A novel two-factor monosynaptic TRIO tracing method for assessment of circuit integration of hESC-derived dopamine transplants
Author
Summary, in English
Transplantation in Parkinson's disease using human embryonic stem cell (hESC)-derived dopaminergic (DA) neurons is a promising future treatment option. However, many of the mechanisms that govern their differentiation, maturation, and integration into the host circuitry remain elusive. Here, we engrafted hESCs differentiated toward a ventral midbrain DA phenotype into the midbrain of a preclinical rodent model of Parkinson's disease. We then injected a novel DA-neurotropic retrograde MNM008 adeno-associated virus vector capsid, into specific DA target regions to generate starter cells based on their axonal projections. Using monosynaptic rabies-based tracing, we demonstrated for the first time that grafted hESC-derived DA neurons receive distinctly different afferent inputs depending on their projections. The similarities to the host DA system suggest a previously unknown directed circuit integration. By evaluating the differential host-to-graft connectivity based on projection patterns, this novel approach offers a tool to answer outstanding questions regarding the integration of grafted hESC-derived DA neurons.
Department/s
- Human Neural Developmental Biology
- MultiPark: Multidisciplinary research focused on Parkinson´s disease
- Molecular Neuromodulation
- Developmental and Regenerative Neurobiology
- StemTherapy: National Initiative on Stem Cells for Regenerative Therapy
- Medical Microspectroscopy
- Behavioural Neuroscience Laboratory
Publishing year
2022-01-11
Language
English
Pages
159-172
Publication/Series
Stem Cell Reports
Volume
17
Issue
1
Document type
Journal article
Publisher
Cell Press
Topic
- Neurosciences
Keywords
- AAV-MNM008
- animal model
- capcid engineering
- Cell replacement
- circuit mapping
- dopamine neurons
- human embryonic stem cells
- monosynaptic tracing
- Parkinson's disease
- retrograde transport
Status
Published
Research group
- Human Neural Developmental Biology
- Molecular Neuromodulation
- Developmental and Regenerative Neurobiology
- Medical Microspectroscopy
- Behavioural Neuroscience Laboratory
ISBN/ISSN/Other
- ISSN: 2213-6711